Drug Repurposing and Orphan Drugs

Repurposing existing drugs offers a faster, cost-effective path to treating rare and neglected diseases. This track begins with a look at successful repurposing stories such as thalidomide and sildenafil, followed by computational tools that predict new indications. Orphan drugs, which target diseases affecting fewer than 200,000 people in the US, are critical yet often underfunded. The session will discuss incentives, fast-tracking opportunities, and challenges in trial design for small populations. Experts will share real-world hurdles in pricing, reimbursement, and post-marketing surveillance of orphan drugs. Discussions will also cover regulatory designations like Orphan Drug Status and Breakthrough Therapy Designation.

A section will be dedicated to public-private partnerships, advocacy groups, and patient-driven initiatives that fuel rare disease research. Case studies will highlight how collaborative approaches accelerate development. Attendees will leave with actionable insights into harnessing drug repurposing and orphan drug pathways to bring life-saving treatments to overlooked patient populations.

    Related Conference of Drug Repurposing and Orphan Drugs

    August 18-19, 2025

    40th World Congress on Pharmacology and Therapeutics

    Valencia, Spain
    August 27-28, 2025

    20th World Congress on Drug Formulation & Drug Delivery

    Amsterdam, Netherlands
    September 19-20, 2025

    18th World Drug Delivery Summit

    Paris, France
    September 22-23, 2025

    Pharma Biotech Expo

    Toronto, Canada
    September 23-24, 2025

    10th International Conference on Future Pharma and Innovations

    Amsterdam, Netherlands
    September 24-25, 2025

    5th World Congress on Rare Diseases & Orphan Drugs

    Aix-en-Provence, France
    October 23-24, 2025

    21st Annual Meet on Pharmaceutical Sciences

    Aix-en-Provence, France
    November 11-12, 2025

    6th Annual Congress on Antibiotics and Bacterial Infections

    Amsterdam, Netherlands
    November 13-14, 2025

    21st International Conference on Pharmaceutical Chemistry

    Aix-en-Provence, France
    November 20-21, 2025

    21st Annual Congress on Pharmacology and Toxicology

    Paris, France
    November 27-28, 2025

    4th World Congress on Precision and Personalized Medicine

    Zurich, Switzerland
    November 27-28, 2025

    4th World Conference on Pharma Industry and Medical Devices

    Zurich, Switzerland
    December 01-02, 2025

    13th International Conference on Clinical Trials

    Vancouver, Canada
    February 23-24, 2026

    3rd World Congress on Biologics and Biosimilars

    London, Aland Islands
    March 23-24, 2026

    36th Annual European Pharma Congress

    London, UK
    April 27-28, 2026

    9th European Biopharma Congress

    Paris, Aland Islands
    May 21-22, 2026

    8th International Conference and Exhibition on Pain Management

    Aix-en-Provence, France
    May 28-29, 2026

    3rd International Conference on Pharmacognosy

    Madrid, Spain

    Drug Repurposing and Orphan Drugs Conference Speakers

      Recommended Sessions

      Related Journals

      Are you interested in